© 2023 澳门正规博彩十大排行平台. All rights reserved.

Independent Research

In alignment with our commitment to scientific innovation and areas of unmet medical need, we may provide product and funding support for independent research in rare diseases and genetic disorders.

This program supports the following types of Investigator Initiated Studies:

  • Clinical studies of approved and investigational uses of 澳门正规博彩十大排行平台 medicines, including medicines approved by the 澳门十大博彩正规游戏平台 or still in development (i.e. interventional studies phase I to IV).
  • Clinical observational studies, real world evidence (i.e. non-interventional studies)
  • Clinical studies requesting 澳门正规博彩十大排行平台 product only

This program does not provide support for animal model studies, CME or non-CME educational activities, event sponsorships, or charitable contributions.

Our medical science staff located throughout the globe are available to guide you through each step in the application process. If you have a concept you would like to submit, please reach out to your Medical Science Liaison (MSL) or Area Medical Director. If you don’t yet have a medical staff contact or for general inquiries, please email us at: independentresearch@bmrn.com

Login and apply for support or review submitted applications
Share Image


About Us

Patients are our purpose. Science is our passion.

Learn More about us